Archive: Sarepta - eteplirsen patient storiesFormerly AVI BioPharma $AVII
This page contains an archive of all media coverage related to Sarepta, eteplirsen, and the boys with DMD enrolled in their clinical trials. Sarepta BiotechDueDiligence Homepage Archive of SRPT investing/stock-focused stories and articles |
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Archive: patient stories in print, online, and television
- July 2011 "Great Ormond Street Hospital Patients Take Part in Duchenne MD Clinical Trial" (Check Orphan)
- "EXON SKIPPING FOR DUCHENNE MUSCULAR DYSTROPHY: A SUCCESSFUL CLINICAL TRIAL IN THE UK" (Action Duchenne)
- October 2011 "Muscular dystrophy treatment: why were the tests not continued?" (The Telegraph UK)
- August 2012 "Clinical Trial shows promise for Jackon 12 year old with Duchenne Muscular Dystrophy" (KFVS - CBS)
- September 2012 "Urgent pleas from parents greet biotech's new drug" (Seattle Times)
- September 2012 "Drug could help boys walk" (Columbus Dispatch)
- September 2012 "MDA Telethon Pittsburgh 2012" (YouTube)
- September 2012 "Exon skipping strategies for the treatment of duplicate mutations in DMD" (CureDuchenne)
- October 2012 "Drug shows promise in treating type of muscular dystrophy in boys" (NY Times)
- October 2012 "The FDA PDUFA patient-focused drug development oportunity" (Duchenne Alliance)
- October 2012 "Sarepta and Eteplirsen" (JETT Foundation)
- October 2012 "Understanding Accelerated Approval" (Parent Project MD)
- October 2012 - Boston Chronicle TV Program on eteplirsen, featuring Sarepta Chief Medical Officer Ed Kaye and the Leclaires, a DMD family (YouTube)
- October 2012 "A Miracle Drug? Hope and Heartache for Families (WCVB Channel 5 Boston)
- October 2012 "Partnering with the FDA to accelerate approvals- The question of risk tolerance in the Duchenne community" (Parent Project Muscular Dystrophy - Pat Furlong)
- 11/1/2012 "I've lost two sons in two years to the same illness..." (The Scottish Sun)
- November 2012 "Duchenne Muscular Dystrophy as a model disease for PDUFA-V" (DuchenneAlliance - Carlo Rago)
- November 2012 "Duchenne and the election" (Parent Project Muscular Dystrophy)
- November 2012 "Advocates, Patients Rally To Support Sarepta Early Drug Approval Push" (TheStreet - Adam Feuerstein)
- November 2012 "Experimental drug shows promise for local boy with muscular dystrophy" (wpxi.com)
- November 2012 "The Duchenne Alliance is on a Mission" (Rare Disease Report)
- November 2012 "Saxtons River youth with rare disease shoots first buck" (Brattleboro, VT Reformer)
- November 2012 "Billy Ellsworth Interview Duchenne Muscular Dystrophy Clinical Trial Update" (WPXI Pittsburgh)
- November 2012 "Desperate Vt. Mom Begs FDA to Get Healing Drug for Son" (ABC News and @JennMcnary)
- November 2012 "Vermont family begs FDA for healing drugs" (WPTZ NBC Vermont and @JennMcnary)
- November 2012 "Representing Duchenne at the Congressional Rare Disease Caucus Briefing" (Parent Project MD) - this link features Congressional testimony from the mother of the two non-ambulant boys on the eteplirsen trial
- 12/10/2012 "Mom urges drug approval to help her son" (Rutland Herald)
Continue reading the most recent eteplirsen/DMD patient stories (2013-)